A combination of stem cell and gene therapy is safe for humans and produces a protein that will protect motor neurons for those with amyotrophic lateral sclerosis, according to the first trial. Read the article to learn more.
A new study suggests that the brain should be the primary target in treating amyotrophic lateral scoliosis (ALS) not the spinal cord, flipping a long-standing belief.
The National Health Service has recently granted the use of Zolgensma, the world's most expensive drug, on a 10-month-old boy suffering from severe spinal muscular atrophy.