Gene Therapy Allows Deaf Baby Girl Born With Congenital Defect To Hear Unaided, Offering Hope To Individuals Suffering From Hearing Loss

MEDICINE & HEALTH 05.09.2024 21:34 PM

A deaf baby girl born with auditory neuropathy was able to hear thanks to a revolutionary gene therapy. Read to learn more.

Junk DNA in Birds Inspires New Technique in Inserting Codes Into Genomes, Unlocks Safe and Efficient Gene Therapy

02.23.2024 07:12 AM

A new technique uses retrotransposon from birds to insert genes into the genome, paving the way for improved gene therapy. Find out more about it in this article.

Sickle Cell Disease Treatment: World's First Gene Therapy Gains Approval in UK

11.22.2023 00:53 AM

The world's first gene therapy for sickle cell disease has now been approved in the UK and can be applied to patients of sickle cell disease who are at least 12 years old and meet certain conditions. Read to learn more.

Gene Therapy Injected Into the Brain Suppresses Alcohol Cravings, Shows Potential in Treating Chronic Drinking Problems

08.15.2023 06:40 AM

A study in monkeys reveals that an experimental gene therapy injected into their brains dramatically curbed their cravings for alcohol. Learn more about it in this article.

Butterfly Children With Fragile Skin May Be Treated Using Novel Gene Therapy in Topical Form

06.13.2023 07:08 AM

The Food and Drug Administration has granted approval on the use of Vyjuvek as the first topical gene therapy against dystrophic epidermolysis bullosa. Continue reading to find out more.

Nanosyringe Shows Promising Results for Gene Therapy, Cancer Treatment [Study]

03.30.2023 10:31 AM

Nanosyringe can be used to improve the delivery of gene therapy, according to a new study. Continue reading for more details.

$3.6M Gene Therapy For Metachromatic Leukodystrophy Saves Toddler But Not Her Sister [Report]

02.15.2023 08:00 AM

A multi-million gene therapy saved a toddler diagnosed with metachromatic leukodystrophy. Continue reading for full details.

27-Year-Old Patient Receiving CRISPR Gene Therapy Dies, Sparking Concern in Scientific Community

11.06.2022 01:42 AM

Read on to know why a 27-year-old patient in CRISPR gene therapy study died. The sole participant in a trial testing a novel and contentious gene-editing medicine has passed away from undetermined circumstances.

Gene Therapy Prevents Blindness in Children With Leber Congenital Amaurosis, NPHP5 Deficiency Expained

09.08.2022 22:49 PM

Scientists developed a gene therapy that can help in the prevention of blindness in children. Continue reading to know more about gene rehabilitation.

Stem Cell and Gene Therapy Combination Potential Protective Abilities in Motor Neurons of Patients with Amyotrophic Lateral Sclerosis (ALS)

09.06.2022 00:14 AM

A combination of stem cell and gene therapy is safe for humans and produces a protein that will protect motor neurons for those with amyotrophic lateral sclerosis, according to the first trial. Read the article to learn more.

Tay-Sachs Disease Treatment: Two Children Became First-Ever Successful Gene Therapy, After 14 Years of Development

02.16.2022 11:09 AM

Two babies have recently been reported to have been given the first-ever treatment for a severe neurological disease called Tay-Sachs disease after more than 14 years of development.

Multipurpose Mini CRISPR System Easier to Deliver Into Human Cells for Gene Therapy, Treat Rheumatoid Arthritis, Diverse Ailments

09.05.2021 21:32 PM

Bioengineers reimagine the CRISPR system as a Swiss Army knife by repurposing it to make a mini version for easier cell engineering and gene therapy to treat rheumatoid arthritis and other diverse ailments.

World's Most Expensive Drug: How Can This NHS-Approved Treatment Save Life of 10-Month-Old Boy?

07.13.2021 05:44 AM

The National Health Service has recently granted the use of Zolgensma, the world's most expensive drug, on a 10-month-old boy suffering from severe spinal muscular atrophy.

Polypeptide Nanoparticle Adapts to Gene Therapy Cargo for More Efficient Delivery System

06.11.2021 05:20 AM

Researchers have developed a new nanoparticle vector made from polypeptide-based materials that are adaptable to various therapies, including gene therapy, for a more effective delivery system.

Blind Man Sees Again: First Ever Vision Restored Through Gene Therapy

05.24.2021 21:14 PM

For the first time, a blind man gets to see again and that's because of a gene therapy doctors used to restore the patient's partial vision.

Novel Gene Therapy Seen to Preserve Memory, Learning Functions in Alzheimer’s Disease Patients

05.05.2021 07:24 AM

Researchers at the University of California - San Diego have successfully tested using mouse models a potential gene therapy for Alzheimer's Disease that preserves memory and learning abilities.

Gene Therapy Gives Vision to Visually Impaired Patients Since Childhood, Study Reveals

04.03.2021 21:30 PM

Study findings revealed that gene therapy provided vision to patients suffering from a rare form of genetic form blindness since childhood.

Microneedle Patch Can Deliver Genetic Material to Target Defective Cells

10.07.2020 23:23 PM

A new method of gene therapy involves minimally invasive microneedles. The patch includes genetic material within nanoparticles and can be applied for various clinical uses such as cancers, diseases, and vaccines.

Efficient Gene Silencing is Now Possible: Thanks To Gold-DNA Nanosunflowers

11.07.2019 07:45 AM

A group of reserachers discovered a gene silencing process that help with effictive and efficient delivery of genes. This process, made effective by a gold DNA nanosunflower, can help cure HIV, infertility and even cancer.

Gold Could Be the Key to Making Gene Therapy for HIV, Blood Disorders More Practical

05.27.2019 13:49 PM

It is the first time scientists used a gold nanoparticle loaded with CRISPR to edit genes in a rare but powerful subset of blood stem cells, the source of all blood cells

'Bubble Boy' Babies Freed From Life of Isolation by Experimental Gene Therapy

04.22.2019 10:20 AM

Treatment restores immune-system function in young children with severe disorder. Imagine a life encased in a "bubble", not allowed to breath in, touch, nor taste much of anything.